Area of research
Neurology · Epidemiology
Research interest
Research interests include Myasthenia Gravis and Thymoma, Peripheral Neuropathies and Disorders, Parkinson's Disease and Spinal Disorders, and Inflammatory Myopathies and Dermatomyositis.
Safety and efficacy of arimoclomol for inclusion body myositis: a multicentre, randomised, double-blind, placebo-controlled trial
Identification of genetic risk loci and prioritization of genes and pathways for myasthenia gravis: a genome-wide association study
Clinical Effects of the Self-administered Subcutaneous Complement Inhibitor Zilucoplan in Patients With Moderate to Severe Generalized Myasthenia Gravis
Clinical features of <scp>LRP4</scp>/agrin‐antibody–positive myasthenia gravis: A multicenter study
Epidemiological evidence for a hereditary contribution to myasthenia gravis: a retrospective cohort study of patients from North America
Long‐term safety and efficacy of eculizumab in generalized myasthenia gravis
Long-term effect of thymectomy plus prednisone versus prednisone alone in patients with non-thymomatous myasthenia gravis: 2-year extension of the MGTX randomised trial
Lambert-Eaton Myasthenic Syndrome
A checklist for clinical trials in rare disease: obstacles and anticipatory actions—lessons learned from the FOR-DMD trial
Safety and efficacy of eculizumab in anti-acetylcholine receptor antibody-positive refractory generalised myasthenia gravis (REGAIN): a phase 3, randomised, double-blind, placebo-controlled, multicentre study
Developing standardized corticosteroid treatment for Duchenne muscular dystrophy
Enhancing Clinical Research Professionals’ Training and Qualifications (ECRPTQ): Recommendations for Good Clinical Practice (GCP) training for investigators and study coordinators
Learning from the past: reflections on recently completed myasthenia gravis trials
Randomized Trial of Thymectomy in Myasthenia Gravis
A Genome-Wide Association Study of Myasthenia Gravis
Efficacy of prednisone for the treatment of ocular myasthenia (EPITOME): A randomized, controlled trial
A47: Progress Report on the Development of New Classification Criteria for Adult and Juvenile Idiopathic Inflammatory Myopathies
Predictors of Clinical Improvement in Rituximab‐Treated Refractory Adult and Juvenile Dermatomyositis and Adult Polymyositis
A randomized, double‐blind, placebo‐controlled phase II study of eculizumab in patients with refractory generalized myasthenia gravis
Randomized, Double-Blind, Placebo-Controlled, Crossover, Multicenter, Phase II Study of Eculizumab in Patients with Refractory Generalized Myasthenia Gravis (gMG) (S35.004)