Area of research
Hematology · Immunology
Research interest
Research interests include Platelet Disorders and Treatments, Blood groups and transfusion, Immunodeficiency and Autoimmune Disorders, and Chronic Lymphocytic Leukemia Research.
Efficacy and safety of mitapivat in pediatric patients with pyruvate kinase deficiency who are not regularly transfused: Results from the Phase 3, global, randomized, double-blind, placebo-controlled ACTIVATE-Kids trial
Outcomes of hematopoietic stem cell gene therapy for Wiskott-Aldrich syndrome
Genotype‐phenotype correlation and molecular heterogeneity in pyruvate kinase deficiency
American Society of Hematology 2019 guidelines for immune thrombocytopenia
Second‐line treatments in children with immune thrombocytopenia: Effect on platelet count and patient‐centered outcomes
Comorbidities and Complications in Adults with Pyruvate Kinase Deficiency
Clinical spectrum of pyruvate kinase deficiency: data from the Pyruvate Kinase Deficiency Natural History Study
Prevalence and management of iron overload in pyruvate kinase deficiency: report from the Pyruvate Kinase Deficiency Natural History Study
Physician decision making in selection of second‐line treatments in immune thrombocytopenia in children
Romiplostim in children with immune thrombocytopenia: a phase 3, randomised, double-blind, placebo-controlled study
Thrombopoietin Receptor Agonist Use in Children: Data From the Pediatric ITP Consortium of North America ICON2 Study
Comparison of Bleeding Tools in a Cohort of Pediatric Patients with ITP: Data from the Pediatric ITP Consortium of North America ICON1 Study
Eltrombopag for the treatment of children with persistent and chronic immune thrombocytopenia (PETIT): a randomised, multicentre, placebo-controlled study
Genes Influencing the Development and Severity of Chronic ITP Identified through Whole Exome Sequencing