Area of research
Molecular Biology · Physiology
Research interest
Research interests include Amyloidosis: Diagnosis, Treatment, Outcomes, RNA Interference and Gene Delivery, Alzheimer's disease research and treatments, and Respiratory viral infections research.
Lumasiran, an RNAi Therapeutic for Primary Hyperoxaluria Type 1
Phase 1/2 Study of Lumasiran for Treatment of Primary Hyperoxaluria Type 1
Phase 3 Trial of RNAi Therapeutic Givosiran for Acute Intermittent Porphyria
Effects of Patisiran, an RNA Interference Therapeutic, on Cardiac Parameters in Patients With Hereditary Transthyretin-Mediated Amyloidosis
Phase 1 Trial of an RNA Interference Therapy for Acute Intermittent Porphyria
Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis
Targeting of Antithrombin in Hemophilia A or B with RNAi Therapy
Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study
ALN-RSV01 for prevention of bronchiolitis obliterans syndrome after respiratory syncytial virus infection in lung transplant recipients