Area of research
Hematology · Genetics
Research interest
Research focused on Transplantation and Hematopoietic cell, with related work in Hematopoietic stem cell transplantation, Neurocognitive, Disease. Notable publications include 'A trial of unrelated donor marrow transplantation for children with severe sickle cell disease', 'Hematopoietic stem cell transplantation rescues the hematological, immunological, and vascular phenotype in DADA2', and 'Successful matched sibling donor marrow transplantation following reduced intensity conditioning in children with hemoglobinopathies'.
Base Editing of <i>HBG1</i> and <i>HBG2</i> Promoters for Sickle Cell Disease
Initial Results from the BEACON Clinical Study: A Phase 1/2 Study Evaluating the Safety and Efficacy of a Single Dose of Autologous CD34+ Base Edited Hematopoietic Stem Cells (BEAM-101) in Patients with Sickle Cell Disease with Severe Vaso-Occlusive Crises
Reni-Cel, an Investigational AsCas12a Gene-Edited Cell Medicine, Led to Sustained Hemoglobin Normalization and Increased Fetal Hemoglobin in Patients with Severe Sickle Cell Disease Treated in the RUBY Trial
Prospective PTCTC trial of myeloablative haplo-BMT with posttransplant cyclophosphamide for pediatric acute leukemias
AsCas12a Gene Editing of <i>HBG1/2</i> Promoters with EDIT-301 Results in Rapid and Sustained Normalization of Hemoglobin and Increased Fetal Hemoglobin in Patients with Severe Sickle Cell Disease and Transfusion-Dependent Beta-Thalassemia
Hematopoietic Cell Transplantation Cures Adenosine Deaminase 2 Deficiency: Report on 30 Patients
Neighborhood poverty and pediatric allogeneic hematopoietic cell transplantation outcomes: a CIBMTR analysis
Infections in Infants with SCID: Isolation, Infection Screening, and Prophylaxis in PIDTC Centers
Neurocognitive dysfunction in hematopoietic cell transplant recipients: expert review from the late effects and Quality of Life Working Committee of the CIBMTR and complications and Quality of Life Working Party of the EBMT
Treosulfan, Fludarabine, and Low-Dose Total Body Irradiation for Children and Young Adults with Acute Myeloid Leukemia or Myelodysplastic Syndrome Undergoing Allogeneic Hematopoietic Cell Transplantation: Prospective Phase II Trial of the Pediatric Blood and Marrow Transplant Consortium
Immune Reconstitution and Infection Patterns after Early Alemtuzumab and Reduced Intensity Transplantation for Nonmalignant Disorders in Pediatric Patients
Hematopoietic stem cell transplantation rescues the hematological, immunological, and vascular phenotype in DADA2
Impact of pre‐transplant depression on outcomes of allogeneic and autologous hematopoietic stem cell transplantation
Neurocognitive Dysfunction in Hematopoietic Cell Transplant Recipients: Expert Review from the Late Effects and Quality of Life Working Committee of the Center for International Blood and Marrow Transplant Research and Complications and Quality of Life Working Party of the European Society for Blood and Marrow Transplantation
Clinical risks and healthcare utilization of hematopoietic cell transplantation for sickle cell disease in the USA using merged databases
A trial of unrelated donor marrow transplantation for children with severe sickle cell disease
Successful matched sibling donor marrow transplantation following reduced intensity conditioning in children with hemoglobinopathies
Outcomes after Hematopoietic Stem Cell Transplantation for Children with I-Cell Disease