Area of research
Neurology · Genetics
Research interest
Research focused on Amyotrophic lateral sclerosis and Placebo, with related work in SOD1, Duchenne muscular dystrophy, Post-hoc analysis. Notable publications include 'An antisense oligonucleotide against SOD1 delivered intrathecally for patients with SOD1 familial amyotrophic lateral sclerosis: a phase 1, randomised, first-in-man study', 'Neurological involvement of coronavirus disease 2019: a systematic review', and 'Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial'.
Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
Genotype–phenotype correlations in valosin-containing protein disease: a retrospective muticentre study
Phase <scp>2B</scp> randomized controlled trial of <scp>NP001</scp> in amyotrophic lateral sclerosis: Pre‐specified and post hoc analyses
Randomized phase 2 study of<scp>ACE</scp>‐083, a<scp>muscle‐promoting</scp>agent, in facioscapulohumeral muscular dystrophy
Neurological involvement of coronavirus disease 2019: a systematic review
An antisense oligonucleotide against SOD1 delivered intrathecally for patients with SOD1 familial amyotrophic lateral sclerosis: a phase 1, randomised, first-in-man study
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