Area of research
Pulmonary and Respiratory Medicine · Genetics
Research interest
Research interests include Medicine, Cystic fibrosis, Genetic enhancement, Genome editing, CRISPR, and RNA splicing.
A deep generative model for deciphering cellular dynamics and in silico drug discovery in complex diseases
Computational fluid dynamics of small airway disease in chronic obstructive pulmonary disease
Prime editing functionally corrects cystic fibrosis-causing CFTR mutations in human organoids and airway epithelial cells
Functional restoration of a CFTR splicing mutation through RNA delivery of CRISPR adenine base editor
Nanoblades allow high-level genome editing in murine and human organoids
Assays of CFTR Function In Vitro, Ex Vivo and In Vivo
Allele specific repair of splicing mutations in cystic fibrosis through AsCas12a genome editing
Roadmap for an early gene therapy for cystic fibrosis airway disease
Preparation for a first-in-man lentivirus trial in patients with cystic fibrosis
FK506 reduces neuroinflammation and dopaminergic neurodegeneration in an α-synuclein-based rat model for Parkinson's disease
rAAV-CFTRΔR Rescues the Cystic Fibrosis Phenotype in Human Intestinal Organoids and Cystic Fibrosis Mice
Amniotic Fluid Derived Stem Cells with a Renal Progenitor Phenotype Inhibit Interstitial Fibrosis in Renal Ischemia and Reperfusion Injury in Rats
A Surgical Technique for Homogenous Renal Distribution of Substances in Rats
A Novel Surgical Approach for Intratracheal Administration of Bioactive Agents in a Fetal Mouse Model
A Novel Surgical Approach for Intratracheal Administration of Bioactive Agents in a Fetal Mouse Model