Area of research
Molecular Biology · Genetics
Research interest
Research interests include RNA modifications and cancer, RNA Research and Splicing, Virus-based gene therapy research, and CAR-T cell therapy research.
Neoadjuvant triplet immune checkpoint blockade in newly diagnosed glioblastoma
Fidanacogene Elaparvovec for Hemophilia B — A Multiyear Follow-up Study
Delphi-driven consensus definition for mesenchymal stromal cells and clinical reporting guidelines for mesenchymal stromal cell–based therapeutics
Understanding AAV vector immunogenicity: from particle to patient
Global seroprevalence of neutralizing antibodies against adeno-associated virus serotypes used for human gene therapies
Two-year safety outcomes of iPS cell-derived mesenchymal stromal cells in acute steroid-resistant graft-versus-host disease
Evolutionary dynamics of whole-body regeneration across planarian flatworms
SpliceWiz: interactive analysis and visualization of alternative splicing in R
The next wave of cellular immunotherapies in pancreatic cancer
Recent advances in cancer fusion transcript detection
Exploring the Clinical Utility of Pancreatic Cancer Circulating Tumor Cells
Locoregional delivery of CAR-T cells in the clinic
Illuminating the dark protein-protein interactome
Mapping oncogenic protein interactions for precision medicine
Multiyear Factor VIII Expression after AAV Gene Transfer for Hemophilia A
Anti-Mesothelin CAR T cell therapy for malignant mesothelioma
Mesenchymal Stromal Cells for the Treatment of Graft Versus Host Disease
CTCF as a regulator of alternative splicing: new tricks for an old player
Unique protein interaction networks define the chromatin remodelling module of the NuRD complex
Long-Term Follow-Up of the First in Human Intravascular Delivery of AAV for Gene Transfer: AAV2-hFIX16 for Severe Hemophilia B
Surveying brain tumor heterogeneity by single-cell RNA-sequencing of multi-sector biopsies
Journey to the Center of the Cell: Tracing the Path of AAV Transduction
Macrophage development and activation involve coordinated intron retention in key inflammatory regulators
The changing paradigm of intron retention: regulation, ramifications and recipes
The Immune Microenvironment in Mesothelioma: Mechanisms of Resistance to Immunotherapy
Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia
Cell, tissue and gene products with marketing authorization in 2018 worldwide
Guidelines for whole genome bisulphite sequencing of intact and FFPET DNA on the Illumina HiSeq X Ten
Exosomal lncRNAs and cancer: connecting the missing links
Safety Following Autologous Transplantation with Lentiglobin Gene Therapy for Transfusion-Dependent β-Thalassemia (TDT) in the Northstar Hgb-204 Study