Area of research
Molecular Biology · Genetics
Research interest
Research focused on Capsid and Computational biology, with related work in Genetic enhancement, Myotonic dystrophy, Immune system. Notable publications include 'Identification of a myotropic AAV by massively parallel in vivo evaluation of barcoded capsid variants', 'Efficient CRISPR/Cas9-mediated editing of trinucleotide repeat expansion in myotonic dystrophy patient-derived iPS and myogenic cells', and 'Semirational bioengineering of AAV vectors with increased potency and specificity for systemic gene therapy of muscle disorders'.
Semirational bioengineering of AAV vectors with increased potency and specificity for systemic gene therapy of muscle disorders
Identification of a myotropic AAV by massively parallel in vivo evaluation of barcoded capsid variants
Next-generation muscle-directed gene therapy by in silico vector design
Efficient CRISPR/Cas9-mediated editing of trinucleotide repeat expansion in myotonic dystrophy patient-derived iPS and myogenic cells
A Novel Platform for Immune Tolerance Induction in Hemophilia A Mice