Area of research
Molecular Biology · Genetics
Research interest
Research interests include CRISPR and Genetic Engineering, Virus-based gene therapy research, CAR-T cell therapy research, and RNA Interference and Gene Delivery.
Editing the Sickle Cell Disease Mutation in Human Hematopoietic Stem Cells: Comparison of Endonucleases and Homologous Donor Templates
Site-Specific Gene Editing of Human Hematopoietic Stem Cells for X-Linked Hyper-IgM Syndrome
Analyzing CRISPR genome-editing experiments with CRISPResso
CRISPR/Cas9-Mediated Correction of the Sickle Mutation in Human CD34+ cells
Genetic treatment of a molecular disorder: gene therapy approaches to sickle cell disease
Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells